Project

Precision medicine in inherited blindness using integrated omics in human and animal models

Code
01G02320
Looptijd
01-01-2020 → 31-10-2026
Financiering
Regional and community funding: Special Research Fund
Onderzoeksdisciplines
  • Natural sciences
    • Genetic predisposition
Trefwoorden
Erfelijke blindheid genomica transcriptomica proteomica interactie profilering splicing cis-regulatie iPSC fotoreceptor precursor cel CRISPR/Cas9 modificatie Xenopus tropicalis antisense oligonucleotide behandeling
 
Projectomschrijving

This multidisciplinary project aims (1) to decipher cis-­regulation in human retina by chromatin conformation profiling, and by the study of regulatory elements in a human and animal model;; (2) to design an integrative framework for omics data analysis to explain missing heritability in inherited
blindness;; (3) to design and test antisense oligonucleotide-­based treatments of novel targets, ultimately resulting in precision medicine for inherited blindness.